First FDA Approved Targeted RNA-based Therapy

The U.S. FDA approved the first of its kind targeted RNA-based therapy Onpattro (patisiran) to treat peripheral nerve disease (polyneuropathy) caused from hereditary transthyretin-mediated amyloidosis (hATTR) in adult patients. This is the first FDA approved treatment...

First FDA approved Drug Treatment for Smallpox

Tecovirimat (TPOXX) is the first FDA approved drug treatment of smallpox. In 1980, WHO declared that smallpox was eradicated; however, tecovirimat was developed as a counter to the possible use of smallpox as a bio-weapon. It is the first product awarded a Material...